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公司资料

Pharming Group 股价、新闻与催化剂

股票代码:
PHAR
交易所:
NASDAQ
行业:
Biotechnology
所在地:
United States

股票表现

11.79 USD (+0.60%)

收盘价

最后更新: 2026年8月17日

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市值

股价为何变动

As of Aug 17, 2026, PHAR closed up 0.60% at $11.79. No new same-company headline was identified in the current news window.

公司概览

Global Rare-Disease Company

Pharming Group is a commercial-stage biopharmaceutical company that develops and commercializes small-molecule and biologic medicines for rare, debilitating, and life-threatening diseases. Headquartered in Leiden, the Netherlands, the company operates in the United States and Europe and markets two rare-disease products across multiple international markets.

RUCONEST for Hereditary Angioedema

RUCONEST is an intravenous on-demand treatment for acute attacks of hereditary angioedema. Pharming positions the product for patients with high disease burden, including those experiencing severe or frequent attacks or inadequate outcomes with other on-demand therapies. The franchise is now primarily focused on the US market.

Joenja for APDS

Joenja, or leniolisib, is a targeted treatment for activated PI3K delta syndrome, a rare primary immunodeficiency caused by dysregulated PI3K delta signaling. The product is approved in the United States and an expanding group of international markets, with eligible populations varying by jurisdiction. Pharming combines commercialization with genetic diagnosis and patient-identification programs intended to find previously unrecognized APDS patients.

Leniolisib Expansion Beyond APDS

Pharming is evaluating leniolisib in two Phase 2 studies involving broader primary immunodeficiencies with immune dysregulation. One study enrolls patients with genetically defined disorders linked to altered PI3K delta signaling, while the other focuses on common variable immunodeficiency. The company expects the two studies to inform a single registrational Phase 3 strategy in the broader CVID population.

Mitochondrial-Disease Pipeline

Napazimone, formerly KL1333, is Pharming's pivotal-stage candidate for primary mitochondrial diseases caused by mitochondrial DNA mutations. The FALCON study is evaluating the therapy in adults with symptoms such as fatigue and muscle weakness and represents the company's principal clinical program outside the leniolisib franchise.

未来催化剂

  • FDA PDUFA decision on the Joenja sNDA for certain children aged 4 to 11 years with APDS on October 24, 2026.
  • Topline Phase 2 data for leniolisib in genetically defined primary immunodeficiencies linked to altered PI3K delta signaling in the fourth quarter of 2026.
  • Topline Phase 2 data for leniolisib in CVID with immune dysregulation in the fourth quarter of 2026.
  • Completion of enrollment in the pivotal FALCON study of napazimone in mitochondrial DNA-driven primary mitochondrial diseases during 2026.

近期新闻

  1. 01

    Pharming announces commercial launch of Joenja (leniolisib) in Japan for adult and pediatric patients with APDS aged 4 and older

  2. 02

    Pharming Group to participate in Canaccord Genuity 46th Annual Growth Conference

  3. 03

    Pharming reports second quarter and first half 2026 financial results and revises year-end guidance; strong Joenja momentum and near-term clinical readouts to support broader therapeutic use

  4. 04

    Pharming Group to report second quarter and first half 2026 financial results and provide business update on July 30

  5. 05

    Pharming announces U.S. FDA acceptance of sNDA resubmission for Joenja® (leniolisib) to treat children aged 4 to 11 years with APDS

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