Gene Therapy

Gene Therapy includes companies delivering genetic material to correct, replace, silence, or modulate disease-driving biology. This sector page is useful for following businesses exposed to AAV, lentiviral, non-viral, or editing-enabled approaches across rare and broader diseases.

Why watch Gene Therapy

This page combines a company index, a watch action, and the newest relevant feed items in one place so readers can monitor a biotech theme without scanning each company one by one.

Latest Gene Therapy news

The latest feed items from companies currently grouped under Gene Therapy.

1. 01
   2026-09-18 11:30 EST

   ABEOAbeona Therapeutics® Congratulates Ultragenyx on U.S. FDA Approval of FAYUVI™ Gene Therapy for Sanfilippo Syndrome Type A (MPS IIIA)

   Source: Abeona Therapeutics

2. 02
   2026-09-16 11:30 EST

   ABEOAbeona Therapeutics® Announces Activation of University of Florida Health as Newest Qualified Treatment Center for ZEVASKYN®

   Source: Abeona Therapeutics

3. 03
   2026-09-15 14:21 EST

   GSKGSK to acquire potential best-in-class T cell-engager (TCE) for multiple myeloma from Chimagen Biosciences

   Source: GSK plc

4. 04
   2026-09-15 11:00 EST

   RCKTRocket Pharmaceuticals Announces FDA Alignment on Path to Complete Pivotal Phase 2 Trial of RP-A501 in Danon Disease

   Source: Rocket Pharmaceuticals

5. 05
   2026-09-13 19:30 EST

   GSKGSK presents positive registrational data to potentially expand Jideytro (zidesamtinib) to first-line ROS1-positive non-small cell lung cancer

   Source: GSK plc

6. 06
   2026-09-13 08:00 EST

   GSKRis-Rez reduced risk of death by 54% versus topotecan in patients with relapsed small cell lung cancer in China

   Source: GSK plc

7. 07
   2026-09-11 20:30 EST

   MXCTMaxCyte Reports Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)

   Source: MaxCyte

8. 08
   2026-09-11 18:00 EST

   PHARFDA approves Pharming’s Joenja® as first treatment for children with APDS in the U.S.

   Source: Pharming Group

9. 09
   2026-09-10 07:00 EST

   GSKGSK’s Shingrix (Recombinant Zoster Vaccine) prefilled syringe presentation approved in Japan

   Source: GSK plc

10. 10
    2026-09-09 13:00 EST

    EDITEditas Medicine Reports Inducement Grants to New Chief Medical Officer

    Source: Editas Medicine

11. 11
    2026-09-09 06:00 EST

    PHARPharming Group to participate in September investor conferences

    Source: Pharming Group

12. 12
    2026-09-08 13:00 EST

    SRPTSarepta Therapeutics Announces Recipients of Route 79, The Duchenne Scholarship Program, for the 2026-2027 Academic Year

    Source: Sarepta Therapeutics

13. 13
    2026-09-08 12:59 EST

    SRPTSarepta Therapeutics anuncia a los destinatarios de Route 79, el Programa de Becas de Duchenne, para el año académico 2026-2027

    Source: Sarepta Therapeutics

14. 14
    2026-09-08 12:30 EST

    CRSPCRISPR Therapeutics to Present at the Morgan Stanley 24th Annual Global Healthcare Conference

    Source: CRISPR Therapeutics

15. 15
    2026-09-08 12:00 EST

    NTLAIntellia Therapeutics Announces FDA Acceptance of Biologics License Application with Priority Review for Lonvoguran Ziclumeran (Lonvo-z) for Hereditary Angioedema (HAE)

    Source: Intellia

16. 16
    2026-09-08 11:00 EST

    EDITEditas Medicine Appoints Dan Ory, M.D., as Chief Medical Officer

    Source: Editas Medicine

17. 17
    2026-09-04 20:05 EST

    NTLAIntellia Therapeutics Reports Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)

    Source: Intellia

18. 18
    2026-09-04 12:50 EST

    NTLAIntellia Therapeutics Secures Non-Dilutive Debt Facility with OrbiMed for up to $400 Million

    Source: Intellia

19. 19
    2026-09-04 12:00 EST

    TSHATaysha Gene Therapies Announces Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)

    Source: Taysha Gene Therapies

20. 20
    2026-09-04 12:00 EST

    NTLAIntellia Therapeutics to Present at Morgan Stanley 24th Annual Global Healthcare Conference

    Source: Intellia

Companies in Gene Therapy

38 companies tagged with Gene Therapy.

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