企業プロフィール
Design Therapeutics 株価・ニュース・カタリスト
- ティッカー:
- DSGN
- 取引所:
- NASDAQ
- セクター:
- Biopharma
- 所在地:
- United States
株価パフォーマンス
14.99 USD (-3.66%)
終値
最終更新: 2026年8月21日
635M USD
時価総額
株価変動の要因
As of Aug 21, 2026, DSGN closed down 3.66% at $14.99. No new same-company headline was identified in the current news window.
企業概要
GeneTAC Platform
Design Therapeutics develops GeneTAC small molecules that bind genomic repeat sequences and modulate transcription. The platform is designed either to increase expression of a deficient gene or reduce expression of a toxic mutant gene.
DT-216P2
DT-216P2 is being developed for Friedreich ataxia and is designed to increase endogenous frataxin expression. The Phase 1/2 RESTORE-FA trial measures safety, pharmacokinetics and changes in frataxin RNA and protein in blood and muscle.
DT-168
DT-168 is in a Phase 2 biomarker trial for Fuchs endothelial corneal dystrophy. The study evaluates corneal-endothelium biomarkers in patients already scheduled for transplant surgery.
DT-818
DT-818 is designed to selectively reduce transcription of the mutant DMPK allele in myotonic dystrophy type 1. A Phase 1 multiple-ascending-dose trial will assess safety and correction of disease-associated RNA mis-splicing.
Earlier Genetic-Disease Pipeline
Design is also characterizing GeneTAC candidates for Huntington’s disease and conducting discovery work across additional genomic disorders.
今後のカタリスト
- Initial dosing in the Phase 1 DT-818 trial planned in the first half of 2026, with results expected in 2027.
- DT-216P2 frataxin biomarker update expected in the second half of 2026.
- Phase 2 biomarker data for DT-168 expected in the second half of 2026.
最近のニュース
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類似銘柄
事業成熟度、治療領域、カタリスト傾向が近い同業銘柄です。